Researchers have developed a CRISPR-based method to insert the XIST gene into the extra chromosome 21 in human stem cells, silencing its activity. This proof-of-concept could pave the way for future therapies for Down syndrome.
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CRISPR takes a bold leap toward silencing Down syndrome's extra chromosome

Extra Chromosome 21 chromosome silenced
14 Kb gene length inserted
20 To 40% integration efficiency