Scientists at St. Jude Children's Research Hospital have reversed HNRNPH2-related neurodevelopmental disorder using antisense oligonucleotides (ASOs) in preclinical models.
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Antisense oligonucleotide strategy reverses HNRNPH2-related neurodevelopmental disorder

Antisense Oligonucleotides (ASOs) Treatment approach
Blocks Aberrant HNRNPH2 Protein Production Mechanism
Science Translational Medicine Publication venue